Innovative therapeutics

Products/
Pipeline

Pipeline

BioMarin is actively developing promising first-in-class or best-in-class therapies to treat rare genetic diseases, which mostly affect children.

The company has a growing product pipeline, with multiple clinical and preclinical candidates in development.

BioMarin product pipeline

-Updated 4Q16

Company Strategy

BioMarin seeks to develop product candidates that:

  • Address currently unmet medical needs
  • Suggest a clear-cut development profile
  • Provide an opportunity to be first-in-class or best-in-class
BioMarin

Diseases

Lysosomal Storage Disorders (MPS I, MPS IVA, MPS VI) PKU, LEMS

Products

Vimizim®
Kuvan®
Naglazyme®
Aldurazyme®
Firdapse®

Patient/Physician Support Contact Information

BioMarin RareConnections
Tel: 866.906.6100
Fax: 888.863.3361
E-mail: support@biomarin-rareconnections.com

Global Medical Information

Contact Global Medical Information

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