Innovative therapeutics

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Roadmap to a New Therapy

Roadmap to a new therapy

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Clinical Trial

A Multicenter, Multinational Clinical Assessment Study for Pediatric Patients with Achondroplasia
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Clinical Trial

A Phase 2 Study of BMN 111 to Evaluate Safety, Tolerability, and Efficacy in Children With Achondroplasia (ACH)
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Clinical Trial

Phase 1, two-part, double-blind, placebo-controlled study to evaluate safety, tolerability, and pharmacokinetics of single and multiple doses of BMN 111 administered to healthy adult volunteers.
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Clinical Trial

A Phase 2 Study to Evaluate the Long-Term Safety, Tolerability, and Efficacy of BMN 111 in Children With Achondroplasia.
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