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Providing promising new therapeutics to patients with severe or life-threatening diseases.

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Click here to learn more about Brineura (cerliponase alfa), including full prescribing information and boxed warning.

Click here to learn more about Vimizim (elosulfase alfa), including full prescribing information and boxed warning.

Click here to learn more about Naglazyme (galsulfase), including full prescribing information.

Click here to learn more about Aldurazyme (laronidase),
including full prescribing information and black box warning.

Click here to learn more about Kuvan (sapropterin dihydrochloride) Tablets for Oral Use and Powder for Oral Solution, including full prescribing information.