Improvements and gaps in reaching treatment goals for patients with hereditary angioedema
The contents of this post were first presented at a poster talk during the annual scientific meeting of the American College of Allergy, Asthma & Immunology’s November 2022 symposium. Hereditary angioedema (HAE) is a genetic disorder that results in unpredictable episodes of severe swelling and can be life threatening. The swelling can affect different parts […]
BioMarin Scientist Spotlight: Drs. Sylvia Fong & Soumi Gupta Discuss the Significance of AAV Therapies
By interrogating the human genome, we’ve designed therapies that address the root cause of genetic disease. That’s a guiding principle for how we approach our research at BioMarin, and nowhere is that more true than in our work researching gene therapy. As part of our commitment to expanding our technical expertise, we’re looking into many […]
Howard University Partners with BioMarin on Regulatory Fellowship
At Howard University, we’re focused on providing our students with valuable experiences that prepare them to become future biopharmaceutical industry leaders. When our College of Pharmacy looked to collaborate with an organization to develop a fellowship in Regulatory Affairs, we wanted a partner that not only thinks strategically about the issues facing the pharmaceutical industry […]
Read More read more ⌃Inspired by the HAE Community, committed to helping make an impact
Last week on HAE Day, we joined the community and HAEi in the effort to raise awareness of HAE. The first report of the hereditary form of angioedema was published almost 140 years ago by Sir William Osler. It took 75 years, until 1963, for the biochemical basis of Hereditary Angioedema (HAE) to be elucidated. […]
The unforgettable moments from “The Style Show: A Runway to Empower”
I am still finding it hard to believe that my lifelong dream of the “The Style Show: A Runway to Empower” is now finally a reality. In front of a sold-out room, 17 models of all shapes, sizes and abilities strutted down the runway representing true diversity in all its forms. I can still feel […]
Independent Research Presented at Pediatric Endocrine Society Annual Meeting
BioMarin congratulates Dr. Andrew Dauber, Chief of Endocrinology at Children’s National Hospital in Washington, D.C., who has recently presented independent research to study a BioMarin therapy, in selected genetic causes of short stature.
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