At the Intersection of Science and Art
It should not come as a surprise to anyone that art and science are siblings. Faced with a lump of clay, a potter has a world of infinite possibility at their beck and call. Every revolution of the potter’s wheel is the beginning of a journey, of an experiment. With much trial and error, with […]
Enduring Purpose, Expanding Reach
As we reflect on the progress of the last quarter century, we take this opportunity to also look forward to what’s next for BioMarin. In our continued pursuit to maximize impact for patients, we continue to ask ourselves: what more can we do? The outcome of this ongoing self-assessment has helped bring clarity to how we can best deliver on our purpose – to transform lives through genetic discovery.

Improvements and gaps in reaching treatment goals for patients with hereditary angioedema
The contents of this post were first presented at a poster talk during the annual scientific meeting of the American College of Allergy, Asthma & Immunology’s November 2022 symposium. Hereditary angioedema (HAE) is a genetic disorder that results in unpredictable episodes of severe swelling and can be life threatening. The swelling can affect different parts […]
Read More read more ⌃BioMarin Scientist Spotlight: Drs. Sylvia Fong & Soumi Gupta Discuss the Significance of AAV Therapies
By interrogating the human genome, we’ve designed therapies that address the root cause of genetic disease. That’s a guiding principle for how we approach our research at BioMarin, and nowhere is that more true than in our work researching gene therapy. As part of our commitment to expanding our technical expertise, we’re looking into many […]
Howard University Partners with BioMarin on Regulatory Fellowship
At Howard University, we’re focused on providing our students with valuable experiences that prepare them to become future biopharmaceutical industry leaders. When our College of Pharmacy looked to collaborate with an organization to develop a fellowship in Regulatory Affairs, we wanted a partner that not only thinks strategically about the issues facing the pharmaceutical industry […]
Inspired by the HAE Community, committed to helping make an impact
Last week on HAE Day, we joined the community and HAEi in the effort to raise awareness of HAE. The first report of the hereditary form of angioedema was published almost 140 years ago by Sir William Osler. It took 75 years, until 1963, for the biochemical basis of Hereditary Angioedema (HAE) to be elucidated. […]
Clinical Trials
Our thoughtful approach to clinical trial design enables us to move fast and efficiently while protecting the safety of our patients.
Learn More about our clinical trials ⌃