Science | March 25, 2022

Advancing our understanding of gene therapy research, one publication at a time

Forty years ago, the idea of gene therapy seemed like science fiction. Deliver a genetic blueprint to human cells using modified viruses or other molecular tools?

Science | February 4, 2022

Zeroing in on Therapeutic Drug Targets

Scientific pioneers Lon Cardon and Karol Estrada shed new light on the decades-old question of how to identify optimal drug targets.

Science | January 28, 2022

BioMarin’s Center of Technology empowers scientists with technology, resources, and collaboration

For a scientist, access to cutting-edge technologies, rare resources, and expert support can turn a new idea into a groundbreaking discovery.

Science | November 21, 2021

Meet the Scientist: Christian Vettermann, Ph.D.

In his latest paper, Dr. Vettermann solves a complex problem facing hemophilia A scientists and clinicians for years.

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