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Current Studies


 

Study 165-306

A Phase 3 Multi Center Study to Evaluate the Safety and Efficacy of Subcutaneous Injections of Pegvaliase in Adolescent Subjects (Ages 12-17) with Phenylketonuria Featuring an Open Label Randomized Two Arm (Active vs Diet Only Control) Design

  • Indication

    Phenylketonuria (PKU)

  • Investigational Therapeutic

    BMN 165

  • Study Type

    Phase 3

  • Goal

    Evaluate safety and efficacy of BMN 165 in adolescents with PKU when administered as an Induction/Titration and Maintenance dose regimen.

  • Status

    This study is currently recruiting participants

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Study 165-305

A Phase 3, Open-Label, Multi-Center Study to Assess the Safety and Efficacy of BMN 165 in Japanese Subjects 18 Years of Age and Older With Phenylketonuria

  • Indication

    Phenylketonuria (PKU)

  • Investigational Therapeutic

    BMN 165

  • Study Type

    Phase 3

  • Goal

    The primary objective of the study is to evaluate the efficacy and safety of BMN 165 in Japanese subjects ≥ 18 years of age with PKU when administered as an Induction/Titration and Maintenance dose regimen.

  • Status

    This study is ongoing, but not recruiting participants.

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