Event Registration

Gene Therapy Trials for Hemophilia A: Where We Are and What Comes Next

Join us for a special event to learn about the BioMarin gene therapy clinical trial program for hemophilia A. This virtual event aims to give you a closer look at how the clinical trials were designed and our current progress.


For people with hemophilia A and caregivers:

January 28th, 2021

4:00 pm PT / 7:00 pm ET

For healthcare providers:

January 19th, 2021

4:00 pm PT / 7:00 pm ET

For HCPs, if you are unable to attend this event,
please reach out to your Medical Science Liaison (MSL).


Virtual event

  • 1-hour panel discussion
  • 30-minute live Q&A
Here’s what we’ll discuss
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    A general overview of the clinical trial process

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    A closer look at the gene therapy clinical trial program for hemophilia A and its current progress

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    BioMarin's approach to advocacy for the hemophilia community

Presented By
Dr. Doris Quon

Dr. Quon is board certified in Hematology & Oncology and Internal Medicine. She obtained her M.D., Ph.D. at the UCLA David Geffen School of Medicine and did her Residency in Internal Medicine as well as Fellowship in Hematology-Oncology at UCLA Medical Center. She first began her residency training at the Orthopaedic Hemophilia Treatment Center (OHTC) back in 2000 and is currently the Medical Director of OHTC. She has an active role in coordinating the federally funded Region IX Hemophilia activities for the center and is the Medical Director of the Hemophilia Foundation of Southern California.

Register now for this event

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