Our patients and their caregivers are extraordinary.
Living their daily lives with remarkable strength, their perseverance compels us to work urgently to find therapeutic solutions to address their serious unmet medical needs. Meet some of the exceptional people who we hope will inspire you as they do us.
Hear From Our Patients
For each disease state we seek to treat, there are a number of organizations and resources that provide great insight and support services.Learn More about our resources ⌃
We are committed to helping patients on BioMarin therapies navigate the management of their conditions.Learn More about BioMarin RareConnections ⌃