"My disability gives me my drive." Mitch does not let living with MPS VI stop him from pursuing his many passions.
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Tyler doesn’t let MPS VI interfere with his daily life. "I try to live as normal a life I can and do the things that people my age like to do." Naglazyme (galsulfase) helps him manage his MPS VI so he can focus on achieving his dreams.
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”Everyone has struggles and troubles in their life,” she says. “it’s how we deal with them that matters...“
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“We are literally in a race against time to get ahead of the damage caused by this disease, and as parents, we cannot watch this happen without a fight.”
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Liam used to struggle to keep his Phe levels under control. But now, with Kuvan (sapropterin dihydrochloride), he is better able to manage his PKU. This means he has less to worry about and can just focus on being a kid.
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With five products on the market and a fully-integrated multinational organization in place, BioMarin is providing innovative therapeutics to patients with serious unmet medical needs.