Achondroplasia

Achondroplasia is a rare genetic bone growth condition characterized by disproportionate short stature, curvature of the spine and an enlarged head (macrocephaly). These characteristics may lead to health challenges including reduced breathing for short periods of time (apnea), upper airway obstruction, obesity, hearing loss and dental problems.

Clinical Trials for Achondroplasia

BioMarin has provided unwavering support for the achondroplasia community for more than ten years. The company continues to conduct innovative research to help advance care and treatment options for individuals with achondroplasia. Learn more about our range of achondroplasia-focused clinical trials below.

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VOXZOGO^® (vosoritide)

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Achondroplasia