Clinical Trials for PKU
With more than 15 years of commitment to the PKU community, we have multiple clinical trials that explore both the condition, as well as potential treatment options. Learn more about our range of PKU-focused clinical trials below.
BMN 307 AAV PKU Gene Therapy
Kuvan® (sapropterin dihydrochloride) Tablets and Powder for Oral Solution
PALYNZIQ® (pegvaliase-pqpz) Injection
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