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Unlocking Tomorrows Together

BioMarin continues its more than 20-year history of developing first or best in class therapies for people with rare genetic diseases. Our first approved therapy was inspired by a father who refused to accept that his son’s rare diagnosis lacked a viable therapy. That relentless pursuit to change the course of his son’s future through the power of treatment is still at the core of who we are today.

Learn more about how our patients inspire, drive and shape our work at BioMarin.

PKU Patient - Ryan
Patient Stories

Meet some of the exceptional people whose stories remain at the heart of everything we do.

Learn More about our patients
Image: Patient, Juanito
Patient & Community Support

Treatment is only the beginning.

We are committed to the communities we treat beyond the therapies we develop.

Learn More about our patient and community support