Community support

Independent research (For healthcare professionals only)

Upholding the mission of driving scientific innovation and areas to meet the unmet medical needs, BioMarin provides product and funding support for independent research in rare diseases and genetic disorders, ranging from clinical to observational studies.

Support to the types of investigator initiated studies include:

  • Clinical studies of approved and investigational use of BioMarin medicines, including medicines approved by the FDA or still in development (i.e., interventional studies phase I to IV).
  • Clinical observational studies, real world evidence (i.e., non-interventional studies)
  • Clinical studies requesting BioMarin product only

Please note that this initiative does not provide support for animal model studies, CME or non-CME educational activities, event sponsorships, or charitable contributions.

BioMarin’s medical science staff located throughout the globe are available to guide you through each step in the application process. If you have a concept you would like to submit, please reach out to your Medical Science Liaison (MSL) or Area Medical Director. If you don’t yet have a medical staff contact or for general inquiries, please email us at: