A holistic approach
We are committed to the communities we treat beyond the therapies we develop. From support services to grants and donations to arts programs and school scholarships, we believe in providing patients, their families and their advocates with the tools they need to live their best lives.
Empowering students living with rare disease.Learn More about the RARE Scholars program ⌃
Grants & Donations
We provide a variety of opportunities to further support our patient communities.Learn More about grants and donations ⌃
For each disease state we seek to treat, there are a number of organizations and resources that provide great insight and support services.Learn More about our resources ⌃