Read the latest updates about BioMarin and learn more about our science, our people and the communities we support.
April 17, 2025
April 2, 2025
March 20, 2025
February 25, 2025
February 24, 2025
BioMarin employees around the world came together throughout March to celebrate International Women’s Day and Women’s History Month. Our BioMarin Women’s Alliance (BWA) employee resource group organized employee lunches, coordinated volunteer opportunities and hosted important conversations grounded in the theme #AccelerateAction. Thanks to our BWA colleagues for hosting these Women’s History Month events and furthering our culture of belonging.
Antisense oligonucleotides are small genetic sequences with big potential. By targeting specific sequences of messenger RNA (mRNA), they can fine-tune genetic instructions, helping regulate production of a specific protein in a targeted way. One powerful application is exon skipping – allowing cells to bypass specific genetic sequences and produce a more functional protein. By unleashing the potential of genetic science, our researchers are pushing the boundaries of what’s possible in treating genetically defined conditions.
Our team left the 2025 ACMG Annual Clinical Genetics Meeting inspired and grateful for the chance to connect with members of the scientific, medical and patient communities who share our dedication to improving the lives of those with genetically defined conditions. We’re encouraged by the progress in PKU and skeletal conditions, including achondroplasia, that was highlighted at the meeting. We remain determined to continue following the science to expand our impact for patients who are counting on us.
Meet Kenneth: a dog lover, gamer, 1970s movie aficionado and record collector, who lives his life to the fullest while managing hemophilia A. As Kenneth reflects on his experience growing up and how living with hemophilia has evolved, he is grateful for the global online community that now exists.
